The Lancet
Onasemnogene abeparvovec gene therapy for symptomatic infantile-onset spinal muscular atrophy in patients with two copies of SMN2 (STR1VE): an open-label,...
The Lancet Neurology Fecha de publicación: 1 de abril de 2020 DOI: https://doi.org/10.1016/S1474-4422(21)00001-6 Autores: Prof John W Day, MD , Prof...
